- www.veongen.com
- Business segment: Drug Discovery
- VeonGen Therapeutics GmbH
- Am Klopferspitz 19
- 82152 Planegg
- Germany
- moc.negnoev@ofni

VeonGen Therapeutics GmbH
Dr. Caroline Man Xu, VeonGen Therapeutics GmbH
About VeonGen Therapeutics
VeonGen Therapeutics: Pioneering Gene Therapies for Retinal Diseases
VeonGen Therapeutics, formerly known as ViGeneron, is a Munich-based clinical-stage biotech developing transformative gene therapies for patients with high unmet needs. In 2025, the company rebranded to reflect its shift from discovery to clinical innovation.
Its pipeline includes two first-in-class AAV programs:
- VG801, a dual AAV therapy for Stargardt disease and other ABCA4-related retinopathies, granted FDA Rare Pediatric Disease Designation (RPDD) and now in Phase 1/2 trials with FDA collaboration under the RDEA program.
- VG901, an intravitreal AAV therapy for CNGA1-related retinitis pigmentosa, which also received FDA RPDD in 2025.
VeonGen is redefining what is possible in gene therapy, with the mission to bring hope to patients long without treatment options.
What drives you?
At VeonGen Therapeutics, our drive comes from advancing science into tangible therapies. Building on years of expertise as VeonGen, we are now a clinical-stage company dedicated to addressing inherited retinal diseases with innovative AAV-based gene therapy platforms. What motivates us is the precision of science and the opportunity to pioneer new delivery approaches that expand the potential of gene therapy. Our lead programs, VG801 for Stargardt disease and ABCA4-related retinopathies, and VG901 for CNGA1-related retinitis pigmentosa, represent first-in-class innovations designed to meet high unmet needs. With FDA Rare Pediatric Disease Designations and early clinical trials underway, we remain focused on translating groundbreaking research into rigorous clinical solutions. Our vision is to redefine what is possible in ocular gene therapy and set new standards in the field.
“By advancing novel AAV platforms, VeonGen is translating cutting-edge science into clinical solutions for retinal disorders with high unmet medical need.”
Dr. Caroline Man Xu


